Bamboo represents a community of researchers, clinicians, regulatory scientists, and business professionals committed to providing hope to patients suffering from devastating disease. We are focused on some of the most devastating neurological and neuromuscular diseases that affect children. These diseases typically have no effective medical treatments available.
Our therapeutic approach targets the underlying genetic defects and the hope is that this will alter the course of these diseases. We are driven by the scientists that have advanced these therapies and inspired by the parents that are devoted to finding treatments for their children. Our initial focus is on a range of diseases from Duchenne Muscular Dystrophy (DMD) to lesser known diseases, such as giant axonal neuropathy (GAN), Friedreich’s ataxia (FA), and Canavan disease.